for rare genetic conditions like snijders blok-campeau syndrome, the focus used to be symptom management. gene editing promised to fix the root. but a 6yo, mei, died 7 days after experimental brain therapy in china.
Death in Chinese Gene-Editing Trial Raises Ethical ConcernsA six-year-old girl passed away just seven days after receiving an experimental, brain-directed gene-editing therapy in China for a rare, non-life-threatening genetic disorder. An investigation revealwww.bioworld.com